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De novo revertant fiber formation and therapy testing in a 3D culture model of Duchenne muscular dystrophy skeletal muscle

Majid Ebrahimi, Heta Lad, Aurora Fusto, Yekaterina Tiper, Asiman Datye, Christine T. O. Nguyen, Erik Jacques, Louise A. Moyle, T M Nguyen, Brennen Musgrave, Carolina Chávez-Madero, Anne Bigot, Chun Chen, Scott Turner, Bryan A. Stewart, Elena Pegoraro, Libero Vitiello, Penney M. Gilbert

2021Acta Biomaterialia54 citationsDOI

Topics & Concepts

Duchenne muscular dystrophyDystrophinMyogenesisSarcolemmaMuscular dystrophyITGA7Skeletal muscleMyocyteCell biologyExtracellular matrixBiologyExon skippingPathologyMedicineAnatomyExonGeneticsGeneAlternative splicingMuscle Physiology and Disorders3D Printing in Biomedical ResearchAdditive Manufacturing and 3D Printing Technologies
De novo revertant fiber formation and therapy testing in a 3D culture model of Duchenne muscular dystrophy skeletal muscle | Litcius