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Correction of a CADASIL point mutation using adenine base editors in hiPSCs and blood vessel organoids

Jingwen Wang, Lei Zhang, Guanglan Wu, Jinni Wu, Xinyao Zhou, Xiaolin Chen, Yongxia Niu, Yiren Jiao, Qianyi Liu, Puping Liang, Guang Shi, Xueqing Wu, Junjiu Huang, Xueqing Wu, Junjiu Huang

2023Journal of genetics and genomics/Journal of Genetics and Genomics18 citationsDOI

Topics & Concepts

CADASILLeukoencephalopathyBiologyVascular smooth muscleMutationMural cellNotch signaling pathwayCancer researchCell biologyGeneticsPathologyGeneDiseaseMedicineEndothelial stem cellIn vitroEndocrinologySmooth muscleCerebrovascular and genetic disordersMetalloenzymes and iron-sulfur proteins
Correction of a CADASIL point mutation using adenine base editors in hiPSCs and blood vessel organoids | Litcius