Functional, sustained recovery of hearing in Otoferlin-deficient mice using DB-OTO, a hair-cell-specific AAV-based gene therapy
Yoojin Chung, Seth D. Koehler, Sarah Cancelarich, Tyler M. Gibson, Gabriela Pregernig, Lars Becker, Quynh-Anh Artinian, Joseph Goodliffe, Ning Pan, Tera Quigley, Arun Senapati, Peter Slade, Lillian M. Smith, Kathy S. So, Xichun Zhang, C. Eduardo Corrales, Peter Weber, Lynn E. Macdonald, Brian Zambrowicz, Aris N. Economides, Christos A. Kyratsous, J. C. Burns, Adam T. Palermo, Leah R. Sabin, John K. Lee, Vassili Valayannopoulos, Jonathon P. Whitton, Meghan C. Drummond
Abstract
-related hearing loss.
Topics & Concepts
Dual (grammatical number)Genetic enhancementVector (molecular biology)AudiologyGeneMedicineBiologyGeneticsArtLiteratureRecombinant DNAHearing, Cochlea, Tinnitus, GeneticsRNA regulation and diseaseRNA Interference and Gene Delivery