Litcius/Paper detail

Functional, sustained recovery of hearing in Otoferlin-deficient mice using DB-OTO, a hair-cell-specific AAV-based gene therapy

Yoojin Chung, Seth D. Koehler, Sarah Cancelarich, Tyler M. Gibson, Gabriela Pregernig, Lars Becker, Quynh-Anh Artinian, Joseph Goodliffe, Ning Pan, Tera Quigley, Arun Senapati, Peter Slade, Lillian M. Smith, Kathy S. So, Xichun Zhang, C. Eduardo Corrales, Peter Weber, Lynn E. Macdonald, Brian Zambrowicz, Aris N. Economides, Christos A. Kyratsous, J. C. Burns, Adam T. Palermo, Leah R. Sabin, John K. Lee, Vassili Valayannopoulos, Jonathon P. Whitton, Meghan C. Drummond

2025Molecular Therapy — Methods & Clinical Development10 citationsDOIOpen Access PDF

Abstract

-related hearing loss.

Topics & Concepts

Dual (grammatical number)Genetic enhancementVector (molecular biology)AudiologyGeneMedicineBiologyGeneticsArtLiteratureRecombinant DNAHearing, Cochlea, Tinnitus, GeneticsRNA regulation and diseaseRNA Interference and Gene Delivery