Safety and efficacy of venglustat in GBA1-associated Parkinson's disease: an international, multicentre, double-blind, randomised, placebo-controlled, phase 2 trial
Nir Giladi, Roy N. Alcalay, Gary Cutter, Thomas Gasser, Tanya Gurevich, Günter U. Höglinger, Kenneth Marek, Claudio Pacchetti, Anthony H.V. Schapira, Clemens R. Scherzer, Tanya Simuni, Pascal Minini, S. Pablo Sardi, Michel Peterschmitt
Topics & Concepts
PlaceboMedicineInternal medicinePopulationNeurologyParkinson's diseaseDiseasePhysical therapyAdverse effectRating scalePsychologyPsychiatryPathologyAlternative medicineDevelopmental psychologyEnvironmental healthLysosomal Storage Disorders ResearchCarbohydrate Chemistry and SynthesisParkinson's Disease Mechanisms and Treatments