Spinal muscular atrophy: state of the art and new therapeutic strategies
Sonia Messina, Maria Sframeli, Lorenzo Maggi, Adele D’Amico, Claudio Bruno, Giacomo P. Comi, Eugenio Mercuri
Topics & Concepts
Spinal muscular atrophySMA*MedicineNeurologyNeurosurgeryDiseaseIntensive care medicineTherapeutic approachPhysical medicine and rehabilitationPhysical therapyPathologySurgeryPsychiatryMathematicsCombinatoricsNeurogenetic and Muscular Disorders ResearchRNA modifications and cancerCongenital Anomalies and Fetal Surgery