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Alpha-dystroglycan binding peptide A2G80-modified stealth liposomes as a muscle-targeting carrier for Duchenne muscular dystrophy

Eri Sasaki, Yoshihiro Hayashi, Yuka Kimura, Sanae Sashida, Nobuhito Hamano, Kei Nirasawa, Keisuke Hamada, Fumihiko Katagiri, Yamato Kikkawa, Takaaki Sakai, Akihiro Yoshida, Masahiro Kawada, Shin‐ichi Hirashima, Tsuyoshi Miura, Yoko Endo‐Takahashi, Motoyoshi Nomizu, Yoichi Negishi

2020Journal of Controlled Release17 citationsDOI

Topics & Concepts

LiposomeDuchenne muscular dystrophyGenetic enhancementMuscular dystrophyChemistryDystrophinMolecular biologyGene deliveryCell biologyPharmacologyMedicineBiochemistryBiologyInternal medicineGeneMuscle Physiology and DisordersRNA Interference and Gene DeliveryVirus-based gene therapy research
Alpha-dystroglycan binding peptide A2G80-modified stealth liposomes as a muscle-targeting carrier for Duchenne muscular dystrophy | Litcius