Genome editing approaches to β-hemoglobinopathies

Mégane Brusson, Annarita Miccio

2021Progress in molecular biology and translational science26 citationsDOI

Topics & Concepts

Genome editingCRISPRTranscription activator-like effector nucleaseBiologyFetal hemoglobinZinc finger nucleaseHemoglobinopathyGeneticsComputational biologyGenetic enhancementViral vectorGenomeCas9DiseaseRNA editingThalassemiaGlobinGeneMedicineHemolytic anemiaGene expressionImmunologyRecombinant DNAPathologyFetusPregnancyHemoglobinopathies and Related DisordersCRISPR and Genetic EngineeringMosquito-borne diseases and control