Litcius/Paper detail

Computational identification of small molecules for increased gene expression by synthetic circuits in mammalian cells

M. B. Pisani, F Calandra, Antonio Rinaldi, F. Cella, Francesca Tedeschi, Iolanda Boffa, Diego Vozzi, Nicola Brunetti‐Pierri, Annamaria Carissimo, Francesco Napolitano, Velia Siciliano

2025Nature Communications7 citationsDOIOpen Access PDF

Abstract

Engineering mammalian cells with synthetic circuits drives innovation in next-generation biotherapeutics and industrial biotechnology. However, applications often depend on cellular productivity, which is constrained by finite cellular resources. Here, we harness computational biology to identify drugs that boost productivity without additional genetic modifications. We perform RNA-sequencing on cells expressing an incoherent feed-forward loop (iFFL), a genetic circuit that enhances operational capacity. To find drugs that mimic this effect, we use DECCODE (Drug Enhanced Cell COnversion using Differential Expression), an unbiased method that matches our transcriptional data with thousands of drug-induced profiles. Among the compound candidates, we select Filgotinib, that enhances expression of both transiently and stably expressed genetic payloads across various experimental scenarios and cell lines, including AAV and lentivirus transduction. Our results reveal cell-specific responses, underscoring the context dependency of small-molecule treatments. Altogether, we present a versatile tool for biomedical and industrial applications requiring enhanced productivity from engineered cells. Engineering mammalian cells with synthetic circuits drives innovation in next-generation biotherapeutics and industrial biotechnology. Here the authors use RNA-seq and computational biology to identify drugs that increase engineered cell productivity without genetic edits - Filgotinib proved enhanced gene expression across contexts, offering a powerful tool for biotech applications.

Topics & Concepts

Gene expressionIdentification (biology)Computational biologyGeneSynthetic biologySmall moleculeBiologyRegulation of gene expressionElectronic circuitCell biologyGeneticsPhysicsBotanyQuantum mechanicsCRISPR and Genetic EngineeringCAR-T cell therapy researchViral Infectious Diseases and Gene Expression in Insects