Welcoming the Era of Gene Editing in Medicine
George Q. Daley
Abstract
Recent approvals of exa-cel for treatment of sickle cell disease and transfusion-dependent β-thalassemia mark the dawn of the era of gene editing in medicine. But ensuring access will be challenging.
Topics & Concepts
Genome editingThalassemiaMedicineGeneBiologyGeneticsCRISPRInternal medicineCRISPR and Genetic EngineeringVirus-based gene therapy researchSARS-CoV-2 and COVID-19 Research