Treatment Options in Spinal Muscular Atrophy: A Pragmatic Approach for Clinicians
Sithara Ramdas, Maryam Oskoui, Laurent Servais
Topics & Concepts
Spinal muscular atrophySMA*MedicineClinical trialPhysical medicine and rehabilitationPhysical therapyDiseaseIntensive care medicinePathologyMathematicsCombinatoricsNeurogenetic and Muscular Disorders ResearchRNA modifications and cancerRNA Research and Splicing