Intracerebroventricular Cerliponase Alfa for Neuronal Ceroid Lipofuscinosis Type 2 Disease: Clinical Practice Considerations From US Clinics
Emily de los Reyes, Lenora Lehwald, Erika F. Augustine, Elizabeth Berry‐Kravis, Karen Butler, Natalie Cormier, Scott Demarest, Sam Lu, Jacqueline Madden, Joffre Olaya, Susan See, Amy Vierhile, James W. Wheless, Amy Yang, Jessica Cohen‐Pfeffer, Dorna Chu, Fernanda Leal‐Pardinas, Raymond Wang
Topics & Concepts
MedicineCerebrospinal fluidEnzyme replacement therapyIntensive care medicineDiseaseInternal medicineLysosomal Storage Disorders ResearchGlycogen Storage Diseases and MyoclonusBiomedical Research and Pathophysiology