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FDA-approved drug screening in patient-derived organoids demonstrates potential of drug repurposing for rare cystic fibrosis genotypes

Eyleen de Poel, Sacha Spelier, Marne C. Hagemeijer, Peter van Mourik, S.W.F. Suen, Annelotte M. Vonk, Jesse E. Brunsveld, Georgia N. Ithakisiou, Evelien Kruisselbrink, Hugo Oppelaar, Gitte Berkers, Kate Groot, Sabine Heida-Michel, S.R. Jans, H. van Panhuis, Marleen Bakker, Renske van der Meer, Jolt Roukema, Edward Dompeling, Els J.M. Weersink, Gerard H. Koppelman, Antoni R. Blaazer, J.E. Muijlwijk-Koezen, Cornelis K. van der Ent, Jeffrey M. Beekman

2023Journal of Cystic Fibrosis42 citationsDOIOpen Access PDF

Topics & Concepts

Cystic fibrosisMedicineDrug repositioningDrugRepurposingApproved drugInternal medicinePharmacologyBiologyEcologyCystic Fibrosis Research AdvancesImmunodeficiency and Autoimmune DisordersPhosphodiesterase function and regulation
FDA-approved drug screening in patient-derived organoids demonstrates potential of drug repurposing for rare cystic fibrosis genotypes | Litcius