Modulators of CFTR. Updates on clinical development and future directions
Emmanuelle Bardin, Alexandra Pastor, Michaëla Semeraro, Anita Golec, Kate Hayes, B. Chevalier, Farouk Berhal, Guillaume Prestat, Alexandre Hinzpeter, Christine Gravier‐Pelletier, Iwona Pranke, Isabelle Sermet‐Gaudelus
Topics & Concepts
Cystic fibrosisCystic fibrosis transmembrane conductance regulatorPotentiatorLimitingRegulatorChemistryMutationPopulationClinical trialGenetic enhancementTransmembrane proteinBioinformaticsGenePharmacologyCancer researchInternal medicineMedicineBiologyBiochemistryReceptorEngineeringMechanical engineeringEnvironmental healthCystic Fibrosis Research AdvancesNeonatal Respiratory Health ResearchTracheal and airway disorders