Durability of transgene expression after rAAV gene therapy
Manish Muhuri, David Lévy, Martin Schulz, Douglas M. McCarty, Guangping Gao
Topics & Concepts
Genetic enhancementTransgeneBiologyImmune systemGeneAdeno-associated virusPhenotypeDosingRecombinant DNAImmunologyVector (molecular biology)GeneticsPharmacologyVirus-based gene therapy researchRNA Interference and Gene DeliveryCRISPR and Genetic Engineering