Maralixibat in progressive familial intrahepatic cholestasis (MARCH-PFIC): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
Alexander Miethke, Adib Moukarzel, Gilda Porta, Joshue Covarrubias Esquer, Piotr Czubkowski, Felipe Ordonez, Antonella Mosca, Amal Aqul, Robert H. Squires, Étienne Sokal, Daniel D’Agostino, Ulrich Baumann, Lorenzo D’Antiga, Nagraj Kasi, Nolwenn Laborde, Çiğdem Arıkan, Chuan-Hao Lin, Susan Gilmour, Naveen Mittal, Fang Kuan Chiou, Simon Horslen, Wolf‐Dietrich Huber, Thomas Jaecklin, Tiago Nunes, Anamaria Lascau, Lara Longpre, Douglas Mogul, Will Garner, Pamela Vig, Vera Hupertz, Regino P. González‐Peralta, Udeme D. Ekong, Jane Hartley, Noémie Laverdure, Nadia Ovchinsky, Richard J. Thompson
Topics & Concepts
Progressive familial intrahepatic cholestasisCholestasisPlaceboMedicineGastroenterologyInternal medicineBile acidPathologyLiver transplantationAlternative medicineTransplantationDrug Transport and Resistance MechanismsLiver Diseases and ImmunityPediatric Hepatobiliary Diseases and Treatments