Therapeutic approaches to preserve the musculature in Duchenne Muscular Dystrophy: The importance of the secondary therapies
Giuseppe Angelini, Giada Mura, Graziella Messina
Topics & Concepts
Duchenne muscular dystrophyWastingGenome editingBiologyMuscular dystrophyBioinformaticsClinical trialExon skippingGenomeExonGeneticsGeneEndocrinologyAlternative splicingMuscle Physiology and DisordersTissue Engineering and Regenerative MedicineElectrospun Nanofibers in Biomedical Applications