Litcius/Paper detail

Assessment of efficacy and safety of volanesorsen for treatment of metabolic complications in patients with familial partial lipodystrophy: Results of the BROADEN study

Elif A Oral, Abhimanyu Garg, Joseph A. Tami, Eric A. Huang, Louis O’Dea, H Schmidt, Anatoly Tiulpakov, Ann Mertens, Veronica J. Alexander, Lynnetta M. Watts, Eunju Hurh, Joseph L. Witztum, Richard S. Geary, Sotirios Tsimikas

2022Journal of clinical lipidology69 citationsDOI

Topics & Concepts

MedicineLipodystrophyPediatricsInternal medicineIntensive care medicineFamily medicineHuman immunodeficiency virus (HIV)Antiretroviral therapyViral loadNuclear Structure and FunctionLipid metabolism and disordersClusterin in disease pathology