Dystrophin Immunity after Gene Therapy for Duchenne’s Muscular Dystrophy
Carsten G. Bönnemann, Beth A. Belluscio, Serge Braun, Carl Morris, Teji Singh, Francesco Muntoni
Topics & Concepts
Duchenne muscular dystrophyDystrophinGenetic enhancementImmunityMuscular dystrophyMedicineGeneGeneticsBiologyImmunologyInternal medicineImmune systemMuscle Physiology and DisordersVirus-based gene therapy researchNeuroscience and Neural Engineering