CRISPR/Cas9-based multiplex genome editing of BCL11A and HBG efficiently induces fetal hemoglobin expression
Yuanyuan Han, Xiaoyu Tan, Tingting Jin, Siqi Zhao, Hu Li, Wei Zhang, Ryo Kurita, Yukio Nakamura, Juan Liu, Di Li, Zhaojun Zhang, Xiangdong Fang, Sheng‐Wen Huang
Topics & Concepts
Genome editingCRISPRCas9BiologyFetal hemoglobinMultiplexAmpliconGlobinEnhancerGeneMolecular biologyGene expressionGeneticsComputational biologyPolymerase chain reactionFetusPregnancyHemoglobinopathies and Related DisordersCRISPR and Genetic EngineeringParvovirus B19 Infection Studies