Safety Concerns with Nusinersen, Risdiplam, and Onasemnogene Abeparvovec in Spinal Muscular Atrophy: A Real-World Pharmacovigilance Study
Wei Zhuang, Mei Lu, Ye Wu, Zhehui Chen, Minying Wang, Xudong Wang, Shaoxing Guan, Wanlong Lin
Topics & Concepts
MedicinePharmacovigilanceSpinal muscular atrophyAdverse effectSMA*Odds ratioInternal medicinePediatricsCombinatoricsDiseaseMathematicsNeurogenetic and Muscular Disorders ResearchMuscle Physiology and DisordersAmyotrophic Lateral Sclerosis Research