Voretigene Neparvovec: A Review in RPE65 Mutation-Associated Inherited Retinal Dystrophy
Connie Kang, Lesley J. Scott
Topics & Concepts
RPE65Retinal pigment epitheliumRetinalCis-trans-IsomerasesMedicineGenetic enhancementRetinal DisorderOphthalmologyAsymptomaticAdverse effectInternal medicineBiologyGeneticsGenePeptidylprolyl isomeraseIsomeraseRetinal Development and DisordersRetinal Diseases and TreatmentsRetinal and Optic Conditions