Durable vision improvement after a single treatment with antisense oligonucleotide sepofarsen: a case report

Artur V. Cideciyan, Samuel G. Jacobson, Allen C. Ho, Alexandra V. Garafalo, Alejandro J. Román, Alexander Sumaroka, Arun K. Krishnan, Małgorzata Świder, Michael R. Schwartz, Aniz Girach