Dissecting ELANE neutropenia pathogenicity by human HSC gene editing

Shuquan Rao, Yao Yao, Josias Soares de Brito, Qiuming Yao, Anne H. Shen, Ruth Watkinson, Alyssa L. Kennedy, Steven Coyne, Chunyan Ren, Jing Zeng, Anna Victoria Serbin, Sabine Studer, Kaitlyn Ballotti, Chad E. Harris, Kevin Luk, Christian S. Stevens, Myriam Armant, Luca Pinello, Scot A. Wolfe, Roberto Chiarle, Akiko Shimamura, Benhur Lee, Peter E. Newburger, Daniel E. Bauer