Litcius/Paper detail

Evaluation of elexacaftor–tezacaftor–ivacaftor treatment in individuals with cystic fibrosis and CFTRN1303K in the USA: a prospective, multicentre, open-label, single-arm trial

George M. Solomon, Rachel W. Linnemann, Rachel Rich, Ashleigh Streby, Brian Buehler, Eric Hunter, Kadambari Vijaykumar, William R Hunt, John J. Brewington, András Rab, Shasha Bai, Adrianna Westbrook, Carmel M. McNicholas, Jong In Hong, Candela Manfredi, C. Barillà, Shingo Suzuki, Brian R. Davis, Eric J. Sorscher

2024The Lancet Respiratory Medicine26 citationsDOI

Topics & Concepts

IvacaftorCystic fibrosisMedicineCystic fibrosis transmembrane conductance regulatorClinical trialInternal medicineIntensive care medicineCystic Fibrosis Research AdvancesPediatric health and respiratory diseasesChemical and Physical Studies