Litcius/Paper detail

Huntington’s disease treated for first time using gene therapy

Elie Dolgin

2025Nature13 citationsDOI

Topics & Concepts

DiseaseMedicineGenetic enhancementClinical trialOncologyInternal medicineBioinformaticsMEDLINEGeneRandomized controlled trialIntensive care medicineGenetic Neurodegenerative DiseasesMitochondrial Function and PathologyNeurological disorders and treatments