Differential respiratory function response in paediatric spinal muscular atrophy types 2 and 3 treated with nusinersen over 3 years
Archana Chacko, Peter D. Sly, Robert S. Ware, Brett Dyer, S. Deegan, Nicole Thomas, Leanne Gauld
Topics & Concepts
Spinal muscular atrophyMedicineRespiratory systemAtrophyPhysical medicine and rehabilitationPediatricsInternal medicineDiseaseNeurogenetic and Muscular Disorders ResearchSpinal Dysraphism and MalformationsCraniofacial Disorders and Treatments