Durability of Voretigene Neparvovec for Biallelic RPE65-Mediated Inherited Retinal Disease
Albert M. Maguire, Stephen R. Russell, Daniel C. Chung, Zi‐Fan Yu, Amy Tillman, Arlene V. Drack, Francesca Simonelli, Bart P. Leroy, Kathleen Z. Reape, Katherine A. High, Jean Bennett
Topics & Concepts
MedicineRPE65RetinalGeneticsOphthalmologyRetinal pigment epitheliumBiologyRetinal Development and DisordersLysosomal Storage Disorders ResearchRetinal and Macular Surgery