<i>N</i> -Acetyl- <scp>l</scp> -Leucine and Neurodegenerative Disease
Cynthia J. Tifft
Abstract
This editorial describes the science behind a study of N-acetyl-l-leucine to treat a specific lysosomal storage disorder, Niemann–Pick disease type C.
Topics & Concepts
LeucineDiseaseNeuroscienceChemistryBiochemistryBiologyMedicineAmino acidInternal medicineLysosomal Storage Disorders ResearchParkinson's Disease Mechanisms and TreatmentsGlycogen Storage Diseases and Myoclonus