Comparison of Cas9 and Cas12a CRISPR editing methods to correct the W1282X-CFTR mutation
L. Santos, Karen Mention, Kader Cavusoglu-Doran, David J. Sanz, Mafalda Bacalhau, Miquéias Lopes‐Pacheco, Patrick T. Harrison, Carlos M. Farinha
Topics & Concepts
CRISPRMedicineCystic fibrosisMutationGenome editingComputational biologyGeneticsBiologyGeneInternal medicineCRISPR and Genetic EngineeringCystic Fibrosis Research Advancesbioluminescence and chemiluminescence research