Ruxolitinib treatment of a patient with steroid-dependent severe autoimmunity due to STAT1 gain-of-function mutation
Kunihiko Moriya, Tasuku Suzuki, Nao Uchida, Tomohiro Nakano, S. Katayama, Masahiro Irie, Takeshi Rikiishi, Hidetaka Niizuma, Satoshi Okada, Kohsuke Imai, Yoji Sasahara, Shigeo Kure
Topics & Concepts
RuxolitinibGain of functionAutoimmunityHematologyMedicineInternal medicineMutationImmunologyOncologyBiologyImmune systemGeneticsGeneMyelofibrosisBone marrowImmunodeficiency and Autoimmune DisordersChronic Lymphocytic Leukemia ResearchPlatelet Disorders and Treatments