A deep intronic TCTN2 variant activating a cryptic exon predicted by SpliceRover in a patient with Joubert syndrome
Takuya Hiraide, Kenji Shimizu, Yoshinori Okumura, Sachiko Miyamoto, Mitsuko Nakashima, Tsutomu Ogata, Hirotomo Saitsu
Topics & Concepts
BiologyGeneticsExome sequencingExonIntronJoubert syndromeRNA splicingDeep sequencingGenomeGeneMutationRNAGenetic and Kidney Cyst DiseasesProtist diversity and phylogenyHedgehog Signaling Pathway Studies