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Targeted in vivo delivery of genetic medicines utilizing an engineered lentiviral vector platform results in CAR T and NK cell generation

James I. Andorko, Ronnie M. Russell, Bruce C. Schnepp, Daniel Grubaugh, Karla F Mullen, Aoi Wakabayashi, Léolène J Carrington, Thomas O’Malley, Leticia Kuri-Cervantes, Timothy D. Culp, Philip R. Johnson

2025Molecular Therapy48 citationsDOIOpen Access PDF

Topics & Concepts

In vivoViral vectorGene deliveryVector (molecular biology)LentivirusVirologyGenetic enhancementBiologyComputational biologyGeneticsGeneRecombinant DNAVirusViral diseaseCAR-T cell therapy researchViral Infectious Diseases and Gene Expression in InsectsRNA Interference and Gene Delivery
Targeted in vivo delivery of genetic medicines utilizing an engineered lentiviral vector platform results in CAR T and NK cell generation | Litcius