Longer-term follow-up of nusinersen efficacy and safety in adult patients with spinal muscular atrophy types 2 and 3
Yaara Fainmesser, Vivian E. Drory, Stephan Ben-Shushan, Anat Lavon, Luba Spector, B. S. Abramovich, Alon Abraham
Topics & Concepts
MedicineSpinal muscular atrophyCohortSMA*SurgeryMotor functionLumbarProspective cohort studyPediatricsInternal medicinePhysical medicine and rehabilitationDiseaseMathematicsCombinatoricsNeurogenetic and Muscular Disorders ResearchCongenital Anomalies and Fetal Surgery