Adeno-Associated Virus Vector for Central Nervous System Gene Therapy
Danqing Zhu, Adam J. Schieferecke, Paola A. Lopez, David V. Schaffer
Topics & Concepts
Adeno-associated virusGenetic enhancementViral vectorBiologyGene deliveryGeneGenome editingCentral nervous systemGenomeVector (molecular biology)NeuroscienceComputational biologyBioinformaticsMedicineGeneticsRecombinant DNACRISPR and Genetic EngineeringVirus-based gene therapy researchRNA regulation and disease