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AAV gene therapy for autosomal recessive deafness 9: a single-arm trial

Jieyu Qi, Liyan Zhang, Ling Lü, Fangzhi Tan, Cheng Cheng, Yicheng Lu, Wenxiu Dong, Yinyi Zhou, Xiaolong Fu, Lulu Jiang, Chang Tan, Shanzhong Zhang, Sijie Sun, Huaien Song, Maoli Duan, Dingjun Zha, Yu Sun, Xia Gao, Lei Xu, Fan‐Gang Zeng, Renjie Chai

2025Nature Medicine35 citationsDOI

Topics & Concepts

MedicineGenetic enhancementGeneticsGeneBiologyPediatricsHearing, Cochlea, Tinnitus, GeneticsRNA regulation and diseaseVirus-based gene therapy research
AAV gene therapy for autosomal recessive deafness 9: a single-arm trial | Litcius