AAV gene therapy for autosomal recessive deafness 9: a single-arm trial
Jieyu Qi, Liyan Zhang, Ling Lü, Fangzhi Tan, Cheng Cheng, Yicheng Lu, Wenxiu Dong, Yinyi Zhou, Xiaolong Fu, Lulu Jiang, Chang Tan, Shanzhong Zhang, Sijie Sun, Huaien Song, Maoli Duan, Dingjun Zha, Yu Sun, Xia Gao, Lei Xu, Fan‐Gang Zeng, Renjie Chai
Topics & Concepts
MedicineGenetic enhancementGeneticsGeneBiologyPediatricsHearing, Cochlea, Tinnitus, GeneticsRNA regulation and diseaseVirus-based gene therapy research