Lentiviral gene therapy with reduced-intensity conditioning for sickle cell disease: a phase 1/2 trial
Michael Grimley, Stella M. Davies, Archana Shrestha, Amy Shova, Monika Asnani, Michael Kent, Farzana Sayani, Charles T. Quinn, Omar Niss, Carolyn Lutzko, Parinda A. Mehta, Pooja Khandelwal, Courtney Little, Sharat Chandra, Sydney Felker, Mengna Chi, Theodosia A. Kalfa, Jennifer Knight‐Madden, Paritha Arumugam, Kristie N. Ramos, Scott R. Witting, Teresa Latham, Frederic D. Bushman, Punam Malik
Topics & Concepts
Genetic enhancementMedicineConditioningDiseaseClinical trialOncologyImmunologyInternal medicineGeneBiologyGeneticsStatisticsMathematicsHemoglobinopathies and Related DisordersVirus-based gene therapy researchParvovirus B19 Infection Studies