Elexacaftor/Tezacaftor/Ivacaftor Improved Clinical Outcomes in a Patient with N1303K-CFTR Based on <i>In Vitro</i> Experimental Evidence
Yunjie Huang, Grace Paul, Jesun Lee, Sunitha Yarlagadda, Karen McCoy, Anjaparavanda P. Naren
Abstract
"Elexacaftor/Tezacaftor/Ivacaftor Improved Clinical Outcomes in a Patient with N1303K-CFTR Based on In Vitro Experimental Evidence." American Journal of Respiratory and Critical Care Medicine, 204(10), pp. 1231–1235
Topics & Concepts
IvacaftorMedicineCystic fibrosisIntensive care medicineCystic fibrosis transmembrane conductance regulatorInternal medicineCystic Fibrosis Research AdvancesNeonatal Respiratory Health ResearchTracheal and airway disorders