Litcius/Paper detail

Engineering a photoactivatable A-to-I RNA base editor for gene therapy in vivo

Huiying Li, Yuhao Qiu, Bowen Song, Xinyi Quan, Dan Zhang, Xinru Li, Jingyun Yang, Xiaohong Liu, Zhiyang Zeng, Jing Ji, Shuming Yin, Qi Dai, Liren Wang, Honghui Han, Haifeng Ye, Zhenliang Sun, Yiyun Cheng, Xueli Zhang, Bing Du, Mingyao Liu, Dali Li

2025Nature Biotechnology10 citationsDOI

Topics & Concepts

Genetic enhancementIn vivoRNAComputational biologyBase (topology)GeneChemistryCancer researchMedicineBiologyGeneticsMathematicsMathematical analysisRNA Interference and Gene DeliveryCRISPR and Genetic EngineeringRNA and protein synthesis mechanisms