Litcius/Paper detail

Enhancing pediatric access to cell and gene therapies

Crystal L. Mackall, Catherine M. Bollard, Nancy L. Goodman, Casey Carr, Rebecca Gardner, Rayne H. Rouce, Elena Sotillo, Rich Stoner, Fyodor D. Urnov, Alan S. Wayne, Julie Park, Donald B. Kohn

2024Nature Medicine33 citationsDOI

Topics & Concepts

BiopharmaceuticalDrug developmentBusinessInvestment (military)Market accessMedicineRisk analysis (engineering)BiotechnologyIntensive care medicineDrugPharmacologyPolitical scienceBiologyAgriculturePoliticsEcologyLawCAR-T cell therapy researchBiomedical and Engineering EducationBiomedical Ethics and Regulation