Gene therapy for β-thalassemia: current and future options
Giulia Hardouin, Annarita Miccio, Mégane Brusson
Topics & Concepts
ThalassemiaGenetic enhancementGenome editingCRISPRTransplantationMedicineHematopoietic stem cell transplantationBioinformaticsBiologyGeneGeneticsInternal medicineCRISPR and Genetic EngineeringHemoglobinopathies and Related DisordersViral gastroenteritis research and epidemiology