Litcius/Paper detail

siRNAs—A New Class of Medicines

Anastasia Khvorova

2023JAMA15 citationsDOI

Abstract

This Genomics and Precision Health article explains how small interfering RNA can modulate disease targets considered “undruggable” by small molecules and biologics.

Topics & Concepts

MedicineClass (philosophy)Traditional medicinePharmacologyArtificial intelligenceComputer scienceRNA Interference and Gene DeliveryMicroRNA in disease regulationTelomeres, Telomerase, and Senescence
siRNAs—A New Class of Medicines | Litcius