Nusinersen treatment in adults with severe spinal muscular atrophy: A real-life retrospective observational cohort study
Claire Lefeuvre, M. Brisset, M. Sarlon, Núria Mestres Petit, David Orlikowski, Bernard Clair, T. Thiry, RY Carlier, Hélène Prigent, Gaël Nicolas, Djillali Annane, Pascal Laforêt, Samuel Pouplin
Topics & Concepts
SMA*Spinal muscular atrophySMN1MedicinePopulationQuality of life (healthcare)Retrospective cohort studyCohortPhysical therapyPhysical medicine and rehabilitationInternal medicineDiseaseEnvironmental healthCombinatoricsMathematicsNursingNeurogenetic and Muscular Disorders ResearchAmyotrophic Lateral Sclerosis ResearchHereditary Neurological Disorders