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International consensus guidelines on the implementation and monitoring of vosoritide therapy in individuals with achondroplasia

Ravi Savarirayan, Julie Hoover‐Fong, Keiichi Ozono, Philippe Backeljauw, Valérie Cormier‐Daire, Kristen DeAndrade, Penny Ireland, Melita Irving, Juan Clinton Llerena, Mohamad Maghnie, Margaret Menzel, Nadia Merchant, Klaus Mohnike, Susana Noval Iruretagoyena, Keita Okada, Svein O. Fredwall

2025Nature Reviews Endocrinology20 citationsDOIOpen Access PDF

Topics & Concepts

AchondroplasiaMedicineGuidelineDelphi methodIntensive care medicineMEDLINEFamily medicinePediatricsPathologyStatisticsMathematicsPolitical scienceLawConnective tissue disorders researchPancreatic and Hepatic Oncology ResearchNeonatal Respiratory Health Research
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