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Machine learning–guided optimization of MALT1 inhibitors for diffuse large B-cell lymphoma via QSAR modelling, molecular docking, ADMET profiling, and molecular dynamics simulations

Josiah Joseph Isah, Adamu Uzairu, Sani Uba, Muhammad Tukur Ibrahim

2025Letters in Drug Design & Discovery7 citationsDOIOpen Access PDF

Abstract

Background The paracaspase MALT1(mucosa-associated lymphoid tissue lymphoma translocation protein 1) plays a pivotal oncogenic role in diffuse large B-cell lymphoma (DLBCL). However, many reported inhibitors exhibit suboptimal stability, drug-likeness, and binding persistence. Objective To develop an integrated machine learning and structure-based pipeline to design and optimize potent, synthetically accessible MALT1 inhibitors. Methods Experimentally validated MALT1 inhibitors from ChEMBL (n = 319) were used to build a Random Forest quantitative structure–activity relationship (QSAR) model using RDKit molecular descriptors. Top-ranked candidates were subjected to molecular docking (PDB ID: 6YN8), absorption–distribution–metabolism–excretion–toxicity (ADMET) evaluation, and structure-guided analogue design. Molecular dynamics simulations and Molecular mechanics–generalised Born surface area (MM-GBSA) binding energy analyses were performed to assess conformational stability and protein–ligand interactions. Results The optimized QSAR model achieved strong predictive performance (external R 2 = 0.65). Docking identified compounds 5 and 6 (−9.0 kcal/mol) with hydrogen bonding around LYS360/ALA361 and hydrophobic groove residues. Four generated analogues (5a–5d) showed improved binding, with compound 5a demonstrating the highest affinity (−11.1 kcal/mol), near-complete predicted absorption (∼99 %), synthetic tractability, and improved clearance. MD simulations revealed that 5a maintained lower root-mean-square deviation (RMSD), reduced solvent-accessible surface area (SASA), and stronger hydrogen-bond occupancy compared to parent compound 5. MM-GBSA analysis showed stronger binding free energy for 5a (−86.23 kcal/mol) versus 5 (−77.75 kcal/mol). Conclusion The machine learning–guided integrated framework successfully optimized MALT1 inhibitors, identifying compound 5a as a promising lead scaffold with therapeutic potential to disrupt oncogenic MALT1 signalling in DLBCL, warranting synthesis and experimental evaluation.

Topics & Concepts

ChemistryQuantitative structure–activity relationshipMolecular dynamicschEMBLDocking (animal)Polar surface areaRandom forestLead compoundComputational biologyADMEHydrogen bondBinding siteMolecular modelBinding affinitiesVirtual screeningBiophysicsRational designAccessible surface areaCombinatorial chemistrySmall moleculeMolecular descriptorProtein Data Bank (RCSB PDB)Drug discoveryBiochemistryStereochemistryComputational chemistryPlasma protein bindingActive siteEnzymeHomology modelingPotential energy surfaceMoleculeTarget proteinComputational Drug Discovery MethodsMelanoma and MAPK PathwaysNF-κB Signaling Pathways