Development of Antisense Oligonucleotide Gapmers for the Treatment of Dyslipidemia and Lipodystrophy
Tejal Aslesh, Toshifumi Yokota
Topics & Concepts
Antisense therapyLipodystrophySpinal muscular atrophyExon skippingMedicineGeneticsBioinformaticsBiologyExonOligonucleotideAlternative splicingGeneLocked nucleic acidAntiretroviral therapyVirusViral loadLipid metabolism and disordersRNA modifications and cancerPeroxisome Proliferator-Activated Receptors