Sickle cell disease landscape and challenges in the EU: the ERN-EuroBloodNet perspective
María Del Mar Mañú Pereira, Raffaella Colombatti, Federico Álvarez, Pablo Bartolucci, Celeste Bento, Angelo Loris Brunetta, Elena Cela, Soteroula Christou, Anna Collado Gimbert, Mariane de Montalembert, Laurence Dedeken, Pierre Fenaux, F. Galactéros, Andreas Glenthøj, Victoria Gutiérrez Valle, Antonis Kattamis, Joachim B. Kunz, Stephan Lobitz, Corrina McMahon, Mariangela Pellegrini, Sara Reidel, Giovanna Russo, Miriam Santos Freire, Eduard J. van Beers, Petros Kountouris, Béatrice Gulbis
Topics & Concepts
MedicineRare diseaseDiseaseEpidemiologyEuropean unionOrphan drugFamily medicinePediatricsEnvironmental healthPathologyBusinessBioinformaticsEconomic policyBiologyHemoglobinopathies and Related DisordersIron Metabolism and DisordersMyeloproliferative Neoplasms: Diagnosis and Treatment