CRISPR/Cas correction of muscular dystrophies
Yu Zhang, Takahiko Nishiyama, Eric N. Olson, Rhonda Bassel‐Duby
Topics & Concepts
CRISPRGenome editingBiologyMuscular dystrophyDuchenne muscular dystrophyMuscle disorderComputational biologyCas9GeneticsGenomeBioinformaticsGeneMedicineInternal medicineCRISPR and Genetic EngineeringGenetics, Aging, and Longevity in Model OrganismsPluripotent Stem Cells Research