Hereditary transthyretin amyloid neuropathies: advances in pathophysiology, biomarkers, and treatment
David Adams, Yoshiki Sekijima, Isabel Conceição, Márcia Waddington‐Cruz, Michael Polydefkis, Andoni Echaniz‐Laguna, Mary M. Reilly
Topics & Concepts
TransthyretinPathophysiologyAmyloid (mycology)MedicineNeuroscienceBioinformaticsPathologyBiologyAmyloidosis: Diagnosis, Treatment, OutcomesCellular transport and secretionProtein Kinase Regulation and GTPase Signaling