In vivo application of base and prime editing to treat inherited retinal diseases
Dong Hyun Jo, Sangsu Bae, Seokjoong Kim, Jin‐Soo Kim, Jeong Hun Kim
Topics & Concepts
CRISPRGenome editingCas9BiologyGeneGeneticsComputational biologyPalindromeSubgenomic mRNAGenomeGuide RNACRISPR and Genetic EngineeringRetinal Development and DisordersCytomegalovirus and herpesvirus research