Combination HSCT and intravenous AAV-mediated gene therapy in a canine model proves pivotal for translation of Krabbe disease therapy

Allison M. Bradbury, Jessica Bagel, Gary P. Swain, Keiko Miyadera, Jill P. Pesayco, Charles‐Antoine Assenmacher, Becky K. Brisson, Ian J. Hendricks, Xiao H. Wang, Zackary M. Herbst, Nettie K. Pyne, Patricia M. O’Donnell, G. Diane Shelton, Michael H. Gelb, Neil R. Hackett, Paul Szabolcs, Charles H. Vite, Maria L. Escolar